Presented by Real Chemistry

Rare Disease Revolution: Life Science's New Frontier

Mar 8, 2024

11:30am – 12:30pm CT

For many years, people diagnosed with a rare disease had little hope of treatment because the costs of research and development were so high for such small patient populations. But today, the outlook has shifted and there is a surge of life science companies prioritizing rare disease, like Mucopolysaccharidos I. Join experts and patient advocates to explore how and why the economic incentives have changed, the importance of patient advocacy to expedite research, and innovative approaches benefiting patients. And learn how these factors impact drug development, affordability and patient care.

Programming descriptions are generated by participants and do not necessarily reflect the opinions of SXSW.

photo of Burcu Eryilmaz
photo of Christine Juday
Christine Juday

Real Chemistry

photo of Terri Klein
Terri Klein

National MPS Society

photo of Heidi Ross
Heidi Ross

National Organization For Rare Disorders

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